Genome editing in induced pluripotent stem cells rescues TAF1 levels in X-linked dystonia-parkinsonism

History
Ann Neurol. 2023

Hanssen H, Diesta CCE, Heldmann M, Dy J, Tantianpact J, Steinhardt J, Sauza R, Manalo HTS, Sprenger A, Reyes CJ, Tuazon R, Laabs BH, Domingo A, Rosales RL, Klein C, Münte TF, Westenberger A, Oropilla JQ, Brüggemann N.

Link
https://movementdisorders.onlinelibrary.wiley.com/doi/10.1002/mds.27441